Articles related to PEDIATRIC NEUROLOGY

The study reveals that 10% of patients treated with eli-cel developed hematologic cancer, with an incidence rate of 2.1 per 100 person-years. This finding emphasizes the need for careful monitoring and risk assessment in gene therapy approaches.

Early use of high-efficacy disease-modifying therapies in pediatric-onset MS patients with minimal disability reduces the risk of progression by 59% compared to no treatment.

Recent insights into SUDC highlight the potential role of seizures and hippocampal changes, urging a reevaluation of pediatric health risks and preventive measures in vulnerable age groups.

This landmark study provides crucial insights into the safety of anti-seizure medications during pregnancy, offering both reassurance to prospective mothers and important guidelines for healthcare providers.

This case study highlights the critical role of vitamin B12 testing in diagnosing and treating neuropsychiatric disorders, urging physicians to consider this simple yet often overlooked test.

Discover how AOC 1044’s recent FDA orphan drug designation could revolutionize the treatment landscape for Duchenne muscular dystrophy patients with exon 44 mutations. Stay tuned for upcoming results from the EXPLORE44 trial.